MT2018-18: Sleeping Beauty Transposon-Engineered Plasmablasts for Hurler Syndrome Post Allo HSCT
Last updated on July 2021Recruitment
- Recruitment Status
- Not yet recruiting
- Estimated Enrollment
- Same as current
Summary
- Conditions
- MPS IH, Hurler Syndrome
- Mucopolysaccharidosis Type IH
- Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome)
- Type
- Interventional
- Phase
- Phase 1Phase 2
- Design
- Allocation: Non-RandomizedIntervention Model: Sequential AssignmentMasking: None (Open Label)Primary Purpose: Treatment
Participation Requirements
- Age
- Between 3 years and 8 years
- Gender
- Both males and females
Description
Not Provided
Not Provided
Tracking Information
- NCT #
- NCT04284254
- Collaborators
- Not Provided
- Investigators
- Principal Investigator: Paul Orchard, MD University of Minnesota, Department of Pediatrics
Get Well Soon