Recruitment

Recruitment Status
Active, not recruiting
Estimated Enrollment
30

Summary

Conditions
  • Batten Disease
  • Acute Lymphocytic Leukemia
  • Acute Myelogenous Leukemia
  • Adrenoleukodystrophy
  • Amegakaryocytic Thrombocytopenia
  • Niemann-Pick Disease
  • Diamond Blackfan Anemia
  • Fucosidosis
  • Severe Aplastic Anemia
  • Myelodysplastic Syndrome
  • Gaucher's Disease
  • Mucopolysaccharidosis VI
  • Wolman Disease
  • Krabbe's Disease
  • Metachromatic Leukodystrophy
  • Mucopolysaccharidosis I
Type
Interventional
Phase
Phase 1
Design
Allocation: Non-RandomizedIntervention Model: Single Group AssignmentMasking: None (Open Label)Primary Purpose: Treatment

Participation Requirements

Age
Younger than 55 years
Gender
Both males and females

Description

Not Provided

Not Provided

Tracking Information

NCT #
NCT01586455
Collaborators
Not Provided
Investigators
Principal Investigator: Mitchell S Cairo, MD New York Medical College