Gene Therapy for Metachromatic Leukodystrophy (MLD)
Last updated on July 2021Recruitment
- Recruitment Status
- Active, not recruiting
- Estimated Enrollment
- 8
Summary
- Conditions
- Lysosomal Storage Disease
- Metachromatic Leukodystrophy
- Type
- Interventional
- Phase
- Phase 1Phase 2
- Design
- Allocation: N/AIntervention Model: Single Group AssignmentMasking: None (Open Label)Primary Purpose: Treatment
Participation Requirements
- Age
- Younger than 7 years
- Gender
- Both males and females
Description
Not Provided
Not Provided
Tracking Information
- NCT #
- NCT01560182
- Collaborators
- Ospedale San Raffaele
- Investigators
- Study Director: Orchard Clinical Trials Orchard Therapeutics
Get Well Soon