Recruitment

Recruitment Status
Active, not recruiting
Estimated Enrollment
8

Summary

Conditions
  • Lysosomal Storage Disease
  • Metachromatic Leukodystrophy
Type
Interventional
Phase
Phase 1Phase 2
Design
Allocation: N/AIntervention Model: Single Group AssignmentMasking: None (Open Label)Primary Purpose: Treatment

Participation Requirements

Age
Younger than 7 years
Gender
Both males and females

Description

Not Provided

Not Provided

Tracking Information

NCT #
NCT01560182
Collaborators
Ospedale San Raffaele
Investigators
Study Director: Orchard Clinical Trials Orchard Therapeutics